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Issue Date | Title | Author(s) | Type | Access |
Jul-2015 | Reparação génica de iPSC através do sistema CRISPR/CAS9 | Lopes, Olga Maria da Silva | other | openAccess |
2019 | Restoring brain cholesterol turnover improves autophagy and has therapeutic potential in mouse models of spinocerebellar ataxia | Nóbrega, Clévio David Rodrigues ; Mendonça, Liliana Simões ; Marcelo, Adriana Isabel do Vale ; Lamazière, Antonin; Tomé, Sandra Marisa Oliveira ; Despres, Gaetan; Matos, Carlos A; Mechmet, Fatich; Langui, Dominique; den Dunnen, Wilfred; Almeida, Luís Pereira de ; Cartier, Nathalie; Alves, Sandro José Paiva Fernandes | article | embargoedAccess |
21-Aug-2014 | RNA Interference Mitigates Motor and Neuropathological Deficits in a Cerebellar Mouse Model of Machado-Joseph Disease | Nóbrega, Clévio ; Nascimento-Ferreira, Isabel ; Onofre, Isabel ; Albuquerque, David ; Déglon, Nicole ; Almeida, Luís Pereira de | article | openAccess |
11-Apr-2013 | Role of Brain-Derived Neurotrophic Factor and Mitochondrial Function in Huntington's Disease | Silva, Ana Cristina Rosa da | doctoralThesis | openAccess |
21-Mar-2017 | Role of microRNA deregulation in the pathogenesis of Machado-Joseph disease | Vijayakumar, Udaya Geetha | doctoralThesis | embargoedAccess |
Mar-2016 | Safety profile of the intravenous administration of brain-targeted stable nucleic acid lipid particles | Conceição, Mariana ; Mendonça, Liliana ; Nóbrega, Clévio; Gomes, Célia ; Costa, Pedro ; Hirai, Hirokazu; Moreira, João Nuno ; Lima, Maria C. Pedroso de ; Manjunath, N.; Almeida, Luís Pereira de | article | openAccess |
17-Dec-2020 | SARS-CoV-2 detection methods: where are we now? | Ferreira, Victor Leonel Vieira | masterThesis | embargoedAccess |
2013 | Silencing mutant ataxin-3 rescues motor deficits and neuropathology in Machado-Joseph disease transgenic mice | Nóbrega, Clévio ; Nascimento-Ferreira, Isabel ; Onofre, Isabel ; Albuquerque, David ; Hirai, Hirokazu; Déglon, Nicole ; Almeida, Luís Pereira de | article | openAccess |
11-Sep-2020 | Simple and Fast SEC-Based Protocol to Isolate Human Plasma-Derived Extracellular Vesicles for Transcriptional Research | Gaspar, Laetitia da Silva ; Santana, Magda M. ; Henriques, Carina ; Pinto, Maria M. ; Ribeiro-Rodrigues, Teresa M. ; Girão, Henrique ; Nobre, Rui Jorge ; Almeida, Luís Pereira de | article | openAccess |
2007 | siRNA delivery by a transferrin-associated lipid-based vector: a non-viral strategy to mediate gene silencing | Cardoso, A. L. C. ; Simões, S. ; Almeida, L. P. de ; Pelisek, J. ; Culmsee, C. ; Wagner, E. ; Lima, M. C. Pedroso de | article | openAccess |
Jul-2015 | Síndrome de Down: caracterização e perspectivas futuras | Jorge, Maria Inês Lourenço | other | openAccess |
Apr-2023 | A standardised protocol for blood and cerebrospinal fluid collection and processing for biomarker research in ataxia | Santana, Magda M. ; Gaspar, Laetitia S. ; Pinto, Maria M. ; Silva, Patrick Joel da ; Adão, Diana ; Pereira, Dina ; Ribeiro, Joana Afonso; Cunha, Inês ; Huebener-Schmid, Jeannette; Raposo, Mafalda; Ferreira, Ana F.; Faber, Jennifer; Kuhs, Sandra; Garcia-Moreno, Hector; Reetz, Kathrin; Thieme, Andreas; Infante, Jon; van de Warrenburg, Bart P. C.; Giunti, Paola; Riess, Olaf; Schöls, Ludger; Lima, Manuela ; Klockgether, Thomas; Januário, Cristina ; Almeida, Luís Pereira de | article | openAccess |
8-Jun-2021 | Stress granules, RNA-binding proteins and polyglutamine diseases: too much aggregation? | Marcelo, Adriana ; Koppenol, Rebekah; Almeida, Luís Pereira de ; Matos, Carlos A.; Nóbrega, Clévio | article | openAccess |
15-Jul-2008 | Striatal and nigral pathology in a lentiviral rat model of Machado-Joseph disease | Alves, Sandro ; Régulier, Etienne ; Nascimento-Ferreira, Isabel ; Hassig, Raymonde ; Dufour, Noelle ; Koeppen, Arnulf ; Carvalho, Ana Luísa ; Simões, Sérgio ; Lima, Maria C. Pedroso de ; Brouillet, Emmanuel ; Gould, Veronica Colomer ; Déglon, Nicole ; Almeida, Luís Pereira de | article | openAccess |
1-Aug-2018 | Stroma-derived IL-6, G-CSF and Activin-A mediated dedifferentiation of lung carcinoma cells into cancer stem cells | Rodrigues, Carlos F. D. ; Serrano, Eurico ; Patrício, Maria I.; Val, Mariana; Albuquerque, Patrícia; Fonseca, João ; Gomes, Célia M. F. ; Abrunhosa, Antero ; Paiva, Artur ; Carvalho, Lina ; Botelho, Maria F. ; Almeida, Luís ; Carreira, Isabel M. ; Alpoim, Maria Carmen | article | openAccess |
2019 | Successes and Hurdles in Stem Cells Application and Production for Brain Transplantation | Henrique, Daniel ; Moreira, Ricardo ; Schwamborn, Jens; Almeida, Luís Pereira de ; Mendonça, Liliana | article | openAccess |
Aug-2008 | Surfactants as microbicides and contraceptive agents: a systematic in vitro study | Vieira, Otília V. ; Hartmann, Diego O. ; Cardoso, Carla M. P. ; Oberdoerfer, Daniel ; Baptista, Marta ; Santos, Manuel A. S. ; Almeida, Luis ; Ramalho-Santos, João: | article | openAccess |
2013 | Terapia génica da insuficiência cardíaca: potencial clínico da sobrexpressão da SERCA2a | Oliveira, Diogo Fernando Gonçalves de | masterThesis | openAccess |
17-Sep-2019 | Terapia Génica na Diabetes Mellitus tipo 1 | Branco, Marta Salvado Abreu Castelo | masterThesis | openAccess |
2008 | Tf-lipoplexes for neuronal siRNA delivery: A promising system to mediate gene silencing in the CNS | Cardoso, A. L. C. ; Simões, S. ; Almeida, L. P. de ; Plesnila, N. ; Lima, M. C. Pedroso de ; Wagner, E. ; Culmsee, C. | article | openAccess |