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Issue DateTitleAuthor(s)TypeAccess
127-Jul-2012Calpain-mediated proteolysis of ataxin-3 in Machado-Joseph diseaseSimões, Ana Teresa doctoralThesisembargoedAccess
22012Calpastatin-mediated inhibition of calpains in the mouse brain prevents mutant ataxin 3 proteolysis, nuclear localization and aggregation, relieving Machado–Joseph diseaseSimões, Ana T. ; Gonçalves, Nélio ; Koeppen, Arnulf ; Déglon, Nicole ; Kügler, Sebastian ; Duarte, Carlos Bandeira ; Almeida, Luís Pereira de articleopenAccess
32016Non-invasive viral-mediated gene therapy for Machado-Joseph diseaseSaraiva, Joana Isabel Rajão masterThesisembargoedAccess
42014Calpain inhibition reduces ataxin-3 cleavage alleviating neuropathology and motor impairments in mouse models of Machado-Joseph diseaseSimões, Ana Teresa ; Gonçalves, Nélio ; Nobre, Rui Jorge ; Duarte, Carlos Bandeira ; Almeida, Luís Pereira de articleembargoedAccess
511-Apr-2013Role of Brain-Derived Neurotrophic Factor and Mitochondrial Function in Huntington's DiseaseSilva, Ana Cristina Rosa da doctoralThesisopenAccess