Browsing by Author Matos, Liliana
Results 1 to 3 of 3
Issue Date | Title | Author(s) | Type | Access |
---|---|---|---|---|
10-Aug-2020 | Lysosomal Storage Disease-Associated Neuropathy: Targeting Stable Nucleic Acid Lipid Particle (SNALP)-Formulated siRNAs to the Brain as a Therapeutic Approach | Coutinho, Maria Francisca; Santos, Juliana Inês; Mendonça, Liliana ; Matos, Liliana; Prata, Maria João ; Jurado, Amália ; Lima, Maria C. Pedroso de ; Alves, Sandra | article | openAccess |
21-Apr-2023 | Neurological Disease Modeling Using Pluripotent and Multipotent Stem Cells: A Key Step towards Understanding and Treating Mucopolysaccharidoses | Carvalho, Sofia; Santos, Juliana Inês; Moreira, Luciana ; Gonçalves, Mariana; David, Hugo; Matos, Liliana; Encarnação, Marisa; Alves, Sandra ; Coutinho, Maria Francisca | article | openAccess |
19-Apr-2022 | Splicing Modulation as a Promising Therapeutic Strategy for Lysosomal Storage Disorders: The Mucopolysaccharidoses Example | Santos, Juliana Inês; Gonçalves, Mariana; Matos, Liliana; Moreira, Luciana ; Carvalho, Sofia; Prata, Maria João ; Coutinho, Maria Francisca; Alves, Sandra | article | openAccess |