Browsing by Author Coutinho, Maria Francisca

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Issue DateTitleAuthor(s)TypeAccess
10-Aug-2020Lysosomal Storage Disease-Associated Neuropathy: Targeting Stable Nucleic Acid Lipid Particle (SNALP)-Formulated siRNAs to the Brain as a Therapeutic ApproachCoutinho, Maria Francisca; Santos, Juliana Inês; Mendonça, Liliana ; Matos, Liliana; Prata, Maria João ; Jurado, Amália ; Lima, Maria C. Pedroso de ; Alves, SandraarticleopenAccess
21-Apr-2023Neurological Disease Modeling Using Pluripotent and Multipotent Stem Cells: A Key Step towards Understanding and Treating MucopolysaccharidosesCarvalho, Sofia; Santos, Juliana Inês; Moreira, Luciana ; Gonçalves, Mariana; David, Hugo; Matos, Liliana; Encarnação, Marisa; Alves, Sandra ; Coutinho, Maria FranciscaarticleopenAccess
19-Apr-2022Splicing Modulation as a Promising Therapeutic Strategy for Lysosomal Storage Disorders: The Mucopolysaccharidoses ExampleSantos, Juliana Inês; Gonçalves, Mariana; Matos, Liliana; Moreira, Luciana ; Carvalho, Sofia; Prata, Maria João ; Coutinho, Maria Francisca; Alves, SandraarticleopenAccess